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Initiative „Forschung und Therapie für die Spinale Muskelatrophie“ im Förderverein für die Deutsche Gesellschaft für Muskelkranke e.V. (Initiative SMA)
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Freiburg im Breisgau, Germany (DE)
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Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study (2024)
Günther R, Wurster CD, Brakemeier S, Osmanovic A, Schreiber-Katz O, Petri S, Uzelac Z, et al.
Journal article